Rare disease patients present unique challenges including delays in diagnosis, lack of expertise about the disease, limited data and poorly defined patient pathways.
The unique nature of these rare diseases means communications require innovative approaches to ensure the needs of the rare disease patient are met. This is true in terms of the launch of orphan drugs and their commercialisation.
Communications about these treatments must be delivered in an effective and innovative way, ensuring therapies can be provided to meet the needs of the rare disease patient. These communications are complex and dependent on a number of factors including information, data and evidence, strategy, plan and launch, and patients and stakeholders. This complexity is associated with a number of challenges that need to be overcome. This will ensure patients can access life-changing therapies that are coming to market now and in the future.